This is NOT directly relevant to MND pharmacologically, but it shows that advances are being made elsewhere in gene therapy. But also the cost - $425,000 per year for five years!
https://www.fda.gov/news-events/pres...y-rare-disease
https://www.cnbc.com/2019/05/24/fda-...e-therapy.html
Doug
https://www.fda.gov/news-events/pres...y-rare-disease
https://www.cnbc.com/2019/05/24/fda-...e-therapy.html
Doug
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